New therapy against rare gene defects

On 15th April is the 1st International Pompe Disease Day, a campaign to raise awareness of this rare but severe gene defect. Pompe Disease is only one of more than 40 metabolic disorders that mainly affect children under the age of 10, often with devastating consequences. Now scientists of the European research project EUCLYD setting up new therapeutic methods to tackle these gene defects.

Fuente : http://www.alphagalileo.org/ViewItem.aspx?ItemId=1...